Last Updated | 31 March 2026

CBYL719P12201

A Two-stage Double-blind, Randomized, Placebo-controlled Study to Assess the Efficacy, Safety and Pharmacokinetics of Alpelisib in paediatric and Adult Patients With Lymphatic Malformations Associated With a PIK3CA Mutation.
External Registry
Site Status Queensland Children's Hospital Sydney Children's Hospital
Queensland Children's Hospital (QLD)
John Hunter Children's Hospital (NSW)
Sydney Children's Hospital (NSW)
Monash Health Clayton (VIC)
Royal Children's Hospital (VIC)
Women's and Children's Hospital (SA)
Perth Children's Hospital (WA)
Royal Hobart Hospital (TAS)
Children's Hospital at Westmead (NSW)
Starship Children's Hospital (NZ)
Christchurch Hospital (NZ)
Preparing to Open
Open
Temporarily Closed
Closed
Complete
Adult Sites These sites are not monitored. Status may vary.
Diagnosis Stage Newly Diagnosed, Relapsed/Refractory
National Sponsor Novartis Pharmaceuticals
Open Date 24/11/2023
Conditions Lymphatic Malformations
Patient Range <100 years
Disease Type Soft Tissue and Bone Tumours (Sarcoma)
Study Type Interventional
International Sponsor N/A

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